Nov. 15, 2024
Harvard Scientists Advance Gene Therapy for Usher Syndrome, Achieving Hearing Restoration and Potential Vision Preservation
BOSTON, MASSACHUSSETTS — Researchers at Harvard Medical School (HMS) have made significant progress in developing a gene therapy for Usher syndrome type 1F, a rare genetic disorder characterized by congenital deafness and progressive vision loss. The new approach, detailed in the Journal of Clinical Investigation, demonstrates restored hearing and balance in animal models and holds promise for improving vision in